On a video call in early September, Sarah Tabrizi first saw the data that she and other researchers studying Huntington’s ...
A single-dose gene replacement therapy is found to improve movement ability in children over 2 years of age and teenagers with spinal muscular atrophy, according to research published in Nature ...
Abeona Therapeutics Inc. (Nasdaq: ABEO) today announced the first commercial patient treatment with FDA-approved ZEVASKYN ...
Almost two thirds of patients with a rare form of blood cancer who took part in a clinical trial of a revolutionary new ...
Preliminary results from two trials of the gene therapy exagamglogene autotemcel (exa-cel) suggest the therapy offers an ...
March Bio is continuing enrollment in the Phase 2 trial, with the Independent Data Monitoring Committee's approval to advance to Simon Stage 2 of the Phase 2 trial. The Company anticipates presenting ...
Irish Independent on MSN
Innovative therapy gives hope to patients whose blood cancer ‘seemed incurable’
Almost two thirds of patients with T-cell acute lymphoblastic leukaemia involved in a clinical trial of the treatment are now ...
News Medical on MSN
New T-Cell Gene Therapy Targets Incurable Leukemia
A groundbreaking new treatment using genome-edited immune cells, developed by scientists at UCL (University College London) and Great Ormond Street ...
13h
Patients with previously untreatable blood cancer now disease-free after world-first gene therapy
Patients with a previously untreatable form of blood cancer are now living disease-free after a world-first gene therapy. Alyssa Tapley, 16, became the first patient with an aggressive form of ...
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